Official Title
A Phase 2 Randomized, Observer-Blind, Placebo-Controlled Study to Assess the Safety, Reactogenicity, and Immunogenicity of the SARS CoV-2 Vaccine ARCT-021 in Healthy Adult Participants
Brief Summary

This is a Phase 2, randomized, placebo-controlled, and observer-blind study in healthy adults. The study will evaluate the safety, tolerability, and immunogenicity of the SARS-CoV-2 RNA vaccine candidate against COVID-19: As 2 doses (at two different dose levels), separated by 28 days or as 1 dose In adults 18 years of age and older

Detailed Description

This is a multiregional, multicenter, Phase 2, randomized, observer-blind study designed to
evaluate the safety, reactogenicity, and immunogenicity of the study vaccine in younger and
older adult participants. Enrolled participants will be randomly assigned to receive either
study vaccine ARCT-021 or placebo (sterile saline).

Approximately 600 participants (300 each in younger [18 to <56 years of age in United States
or 21 to <56 years of age in Singapore] and older [≥56 years of age] participants) will be
enrolled (including at least 50% of participants in the older cohort ≥65 years of age).
Participants will be stratified by age and then randomly assigned (3 ARCT-021:1 placebo) to
receive 2 doses of study vaccine separated by 28 days. At 180 days after second study
vaccination (Day 208), participants in Study Groups 1, 2, and 3 will be randomly assigned
again to receive a single booster dose of study vaccine (randomly assigned as 1 ARCT-021:1
placebo). Study Group 4 will not be randomized but will receive 1 dose of placebo at Day 208.
Study Groups are summarized in Table 1. Study vaccine will be administered in an
observer-blind fashion. Participants will be followed for safety and immunogenicity through
180 days after booster vaccination (Day 388). At a subset of clinical sites, all enrolled
participants will also undergo blood sampling for evaluation of CMI responses.

Vaccine doses will be assigned as follows:

Younger Age Cohort:

Study Group 1: n= 75 participants, ARCT-021 7.5 µg (first dose), Placebo (second dose Study
Group 2: n= 75 participants, ARCT-021 5.0 µg (first dose), 5.0 µg (second dose) Study Group
3: n= 75 participants, ARCT-021 7.5 µg (first dose), 7.5 µg (second dose) Study Group 4: n=
75 participants, Placebo (first dose), Placebo (second dose)

Booster Vaccine:

Study Groups 1, 2, 3: 113 participants, ARCT-021 5.0 µg or 7.5 µg, 112 participants, Placebo
Study Group 4: n= 75 participants, Placebo

Older Age Cohort:

Study Group 1: n= 75 participants, ARCT-021 7.5 µg (first dose), Placebo (second dose Study
Group 2: n= 75 participants, ARCT-021 5.0 µg (first dose), 5.0 µg (second dose) Study Group
3: n= 75 participants, ARCT-021 7.5 µg (first dose), 7.5 µg (second dose) Study Group 4: n=
75 participants, Placebo (first dose), Placebo (second dose)

Booster Vaccine:

Study Groups 1, 2, 3: 113 participants, ARCT-021 5.0 µg or 7.5 µg, 112 participants, Placebo
Study Group 4: n= 75 participants, Placebo

A DSMB will be in place to independently review the safety data of participants. Pausing
Rules are also utilized in this study to reduce risk to study participants.

The expected duration of participation for an individual participant is approximately 14
months, inclusive of the Screening period.

Terminated
COVID19
SARS-CoV Infection
Corona Virus Infection

Biological: ARCT-021 single dose priming

ARCT-021 higher dose (one dose) + placebo (one dose)

Biological: ARCT-021 two lower dose priming

ARCT-021 lower dose (two doses, Day 0 and Day 28)

Biological: ARCT-021 two higher dose priming

ARCT-021 higher dose (two doses, Day 0 and Day 28)

Biological: Placebo (two doses), priming

Placebo (two doses, Day 0 and Day 28)

Biological: Randomized booster

ARCT-021 (single dose) OR placebo, booster

Biological: Placebo booster

Placebo (single dose)

Eligibility Criteria

Inclusion Criteria:

Individuals who:

1. are able to provide consent

2. agree to comply with all study visits and procedures

3. are willing and able to adhere to study restrictions

4. are sexually active and willing to adhere to contraceptive requirements

5. are male or female ≥18 or (in Singapore) ≥21 years of age

6. are medically stable

Exclusion Criteria:

Individuals who:

1. have had SARS-CoV-2 infection or COVID-19 disease.

2. have had cancer except for cancers that were treated and that have low risk of
returning

3. have chronic kidney disease

4. have some chronic lung diseases

5. have some heart conditions

6. have compromised immune systems

7. are obese

8. have sickle cell disease or some other blood disorders

9. are current smokers and/or use illegal drugs

10. have Type 2 diabetics

11. are immunocompromised, immunodeficient or have had a transplant

12. have autoimmune disease

13. have other severe or uncontrolled diseases or disease that may interfere with the
interpretation of the study

14. have a positive test for hepatitis B or C or human immunodeficiency virus

15. have had a severe reaction to previous investigational vaccines

16. have a fever or are feeling sick close to the time of the first vaccination of the
study

17. have positive drug test at screening

18. are pregnant

19. are breastfeeding

20. have a bleeding disorder

21. have previously received an investigational coronavirus vaccine (SARS-CoV(1) or MERS)
or who plan to be in other COVID-19 studies

22. have recently been vaccinated with other vaccines

23. have recently received blood products

24. who work at one of the clinic sites participating in this study, work at Arcturus, who
work at other companies that monitor the study or close family members to the sites,
Arcturus, or partners involved in study monitoring

25. other restrictions may apply

Eligibility Gender
All
Eligibility Age
Minimum: 18 Years ~ Maximum: N/A
Countries
Singapore
United States
Locations

Arcturus Investigational Site 103
Chandler, Arizona, United States

Arcturus Investigational Site 107
Tucson, Arizona, United States

Arcturus Investigational Site 112
San Diego, California, United States

Arcturus Investigational Site 104
Melbourne, Florida, United States

Arcturus Investigational Site 105
Orlando, Florida, United States

Arcturus Investigational Site 106
Pinellas Park, Florida, United States

Arcturus Investigational Site 109
The Villages, Florida, United States

Arcturus Investigational Site 101
Peoria, Illinois, United States

Arcturus Investigational Site 110
Rockville, Maryland, United States

Arcturus Investigational Site 102
Anderson, South Carolina, United States

Arcturus Investigational Site 111
Austin, Texas, United States

Arcturus Investigational Site 108
Dallas, Texas, United States

Arcturus Investigational Site 204
Singapore, Singapore

Arcturus Investigational Site 201
Singapore, Singapore

Arcturus Investigational Site 203
Singapore, Singapore

Arcturus Therapeutics, Inc.
NCT Number
Keywords
SARS-CoV-2 Vaccine
Coronavirus Virus Diseases
RNA COVID 19
COVID 19 Vaccine Arcturus
self amplifying RNA vaccine
MeSH Terms
Infections
Communicable Diseases
COVID-19
Coronavirus Infections
Severe Acute Respiratory Syndrome