Official Title
A Phase 2/3, Randomized, Double-blind, Placebo-controlled Study to Evaluate the Efficacy and Safety of Mavrilimumab (KPL-301) Treatment in Adult Subjects Hospitalized With Severe COVID-19 Pneumonia and Hyper-inflammation
Brief Summary

Interventional, randomized, double-blind, placebo-controlled study encompassing 2 development phases (Phase 2 and Phase 3).

Detailed Description

The Phase 2 portion of the study will evaluate the efficacy and safety of 2 dose levels of
mavrilimumab relative to placebo (standard of care) in participants who have tested positive
for severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2) with x-ray/computed
tomography (CT) evidence of bilateral pneumonia and active or recent signs of
hyperinflammation (fever or clinical laboratory results indicative of hyper-inflammation).
The Phase 3 portion is intended to confirm Phase 2 efficacy and safety findings. In both
Phase 2 and Phase 3, participants will be enrolled into 2 cohorts: Cohort 1 will include
non-intubated, hospitalized participants who require supplemental oxygen to maintain oxygen
saturation (SpO2) ≥ 92% (ie, "non-ventilated" participants); Cohort 2 will include
hospitalized participants for whom mechanical ventilation was recently initiated (ie,
"ventilated" participants). Following Screening, enrolled participants in each cohort will be
randomized 1:1:1 to receive one of 2 mavrilimumab dose levels, or placebo as a single
intravenous (IV) infusion (Day 1). Participants will undergo primary study assessments
through Day 29 and will be followed for safety through Day 90.

Completed
COVID

Drug: mavrilimumab

anti-granulocyte-macrophage colony-stimulating factor receptor alpha (GM-CSF-Rα) monoclonal antibody (human isoform immunoglobulin G [IgG4])
Other Name: (KPL-301; CAM3001)

Other: Placebo

matching placebo

Eligibility Criteria

Key Inclusion Criteria:

- Subject (or legally authorized representative) is able and willing to provide informed
consent, which includes compliance with study requirements and restrictions listed in
the consent form. Consent must be performed per institutional regulations.

- Age of ≥ 18 years

- Positive SARS-CoV-2 (2019-nCoV) test within 14 days prior to randomization

- Hospitalized for SARS-CoV-2 (2019-nCoV)

- Bilateral pneumonia on chest x-ray or computed tomography

- Clinical laboratory results indicative of hyper-inflammation within 7 days prior to
randomization

- Cohort 1: Receiving any form of non-invasive ventilation OR oxygenation to maintain
SpO2 ≥ 92% and non-mechanically ventilated (examples include nasal cannula, face mask,
venturi mask, high-flow nasal cannula, or non-invasive positive pressure ventilation)

- Cohort 2: Recently ventilated with mechanical ventilation beginning within 48 hours
prior to randomization

Key Exclusion Criteria:

- Onset of COVID-19 symptoms > 14 days prior to randomization

- Hospitalized > 7 days prior to randomization

- Need for invasive mechanical ventilation (Only for Cohort 1)

- Need for ECMO

- Serious prior or concomitant illness that in the opinion of the Investigator precludes
the subject from enrolling in the trial

- Recent treatment with cell-depleting biological therapies (eg, anti-CD20) within 12
months, non-cell-depleting biological therapies (such as anti-tumor necrosis factor
[TNF], anakinra, anti-IL-6 receptor [eg, tocilizumab], or abatacept) within 8 weeks
(or 5 half-lives, whichever is longer), treatment with alkylating agents within 12
weeks, treatment with cyclosporine A, azathioprine, cyclophosphamide, mycophenolate
mofetil (MMF), or other immunosuppressant (except for corticosteroids) within 4 weeks
prior to randomization. Medications that become standard of care for COVID-19 and/or
receive emergency use authorization may be allowed after discussion with the medical
monitor.

- If subject is receiving or has received hydroxychloroquine within 3 months prior to
screening visit, a corrected QT interval by Federicia method (QTcF) on Screening
electrocardiogram (ECG) ≥500ms is exclusionary. If subject has a pacemaker, this
criterion does not apply.

- Enrolled in another investigational study of a medical intervention within 30 days
prior to randomization. Participation in open label trials involving investigational
treatments for COVID-19 may be allowed upon approval by the Sponsor.

- Life expectancy less than 48 hours, in the opinion of the Investigator

- Known human immunodeficiency virus infection (regardless of immunological status),
known hepatitis B virus surface antigen positivity and/or anti-hepatitis C virus
positivity

Eligibility Gender
All
Eligibility Age
Minimum: 18 Years ~ Maximum: N/A
Countries
Brazil
Chile
Peru
South Africa
United States
Locations

UCLA Medical Center
Los Angeles, California, United States

SHARP Health Care
San Diego, California, United States

Affinity Health
Chicago, Illinois, United States

Tulane University School of Medicine
New Orleans, Louisiana, United States

Allina Health System
Minneapolis, Minnesota, United States

Mercy Clinic Hospitalists
Springfield, Missouri, United States

University of Cincinnati
Cincinnati, Ohio, United States

Bryn Mawr Hospital
Bryn Mawr, Pennsylvania, United States

University of Texas Health Sciences
Houston, Texas, United States

Hospital Cardio Pulmonar
Salvador, Bahia, Brazil

Hospital Luxemburgo - Associação Mário Penna
Belo Horizonte, Minas Gerais, Brazil

CPCLIN - Centro de Pesquisas Clínicas
Natal, Rio Grande Do Norte, Brazil

Hospital Bruno Born
Lajeado, Rio Grande Do Sul, Brazil

UPECLIN - Unidade de Pesquisa Clínica
Botucatu, Sao Paulo, Brazil

IPECC - Instituto de Pesquisa Clínica de Campinas
Campinas, Sao Paulo, Brazil

Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto da Universidade de São Paulo
Ribeirão Preto, São Paulo, Brazil

Hospital Adventista de Belem
Belém, Brazil

IEP HGF - Instituto de Estudos e Pesquisas Clinicas do Ceará
Fortaleza, Brazil

Fundação Faculdade Regional de Medicina de São José do Rio Preto
São José, Brazil

Hospital Alemão Oswaldo Cruz
São Paulo, Brazil

Clinica Las Condes
Santiago, Chile

Hospital Clinico Universidad de Chile
Santiago, Chile

Hospital Nacional Alberto Sabogal Sologuren
Bellavista, Peru

Essalud - Hospital de Emergencias Grau
Lima Cercado, Peru

Hospital Nacional Cayetano Heredia
San Martín De Porres, Peru

Clinica Providencia
San Miguel, Peru

University of Cape Town - Lung Institute
Cape Town, Western Cape, South Africa

IATROS International
Bloemfontein, South Africa

Tiervlei Trial Center
Cape Town, South Africa

TASK Eden
George, South Africa

Into Research - Little Company of Mary Medical Center
Pretoria, South Africa

Limpopo Clinical Research Initiative
Rustenburg, South Africa

Kiniksa Pharmaceuticals, Ltd.
NCT Number
Keywords
Covid-19
Pneumonia
hyper-inflammation
MeSH Terms
COVID-19
Pneumonia
Inflammation
Mavrilimumab